Our Call for Research nr. 12 is now open!
This new Call for SMA research projects is open to research proposals that address the needs of people who live with SMA and demonstrate a clear pathway to impacting those in the short or longer term.
We are happy to share the latest Community Letter issued by Roche.
We are pleased to share with you the latest Community Update from Biogen.
Background and Objectives of the publication.
Spinal muscular atrophy (SMA) is a progressive neuromuscular disorder associated with continuous motor function loss and complications, such as scoliosis and contractures. Understanding the natural history of SMA is key to demonstrating the long-term outcomes of SMA treatments. This study reviews the natural history of motor function, scoliosis, and contractures in patients with SMA.