EUPESMA 2023 Survey is now rolling!
The Pan-European Survey on SMA and Clinical Trials is live!
What would you like to see in future clinical trials for SMA?
Help us advocate for clinical trials that meet the needs of people living with SMA!
The Pan-European Survey on SMA and Clinical Trials is live!
What would you like to see in future clinical trials for SMA?
Help us advocate for clinical trials that meet the needs of people living with SMA!
We are pleased to share with you the latest Community Update from Roche.
We are delighted to share with all of you the latest article about our 2023 Awareness Campaign: "I am Unique".
Background and Objectives of the publication.
Spinal muscular atrophy (SMA) is a progressive neuromuscular disorder associated with continuous motor function loss and complications, such as scoliosis and contractures. Understanding the natural history of SMA is key to demonstrating the long-term outcomes of SMA treatments. This study reviews the natural history of motor function, scoliosis, and contractures in patients with SMA.